Evaluation of long-term effectiveness of the use of carglumic acid in patients with propionic acidemia (PA) or methylmalonic acidemia (MMA): study protocol for a randomized controlled trial

Journal article

Open access

Peer reviewed

BMC pediatrics, Vol.19(1), pp.195-195

13/06/2019

PMCID: PMC6563377

PMID: 31196016

Abstract

Carbaglu

Carglumic acid

Hyperammonemia

Methylmalonic acidemia

Propionic acidemia

Study Protocol

url

https://doi.org/10.1186/s12887-019-1571-yView

Published (Version of record) Open

1 Record Views

Title: Evaluation of long-term effectiveness of the use of carglumic acid in patients with propionic acidemia (PA) or methylmalonic acidemia (MMA): study protocol for a randomized controlled trial
Creators - without role: Marwan Nashabat - King Saud bin Abdulaziz University for Health Sciences
Abdulrahman Obaid - National Guard Health Affairs
Fuad Al Mutairi - King Saud bin Abdulaziz University for Health Sciences
Mohammed Saleh - King Fahd Medical City
Mohammed Elamin - King Fahd Medical City
Hind Ahmed - King Abdulaziz Medical City
Faroug Ababneh - King Abdulaziz Medical City
Wafaa Eyaid - King Saud bin Abdulaziz University for Health Sciences
Abdulrahman Alswaid - King Saud bin Abdulaziz University for Health Sciences
Lina Alohali - King Saud bin Abdulaziz University for Health Sciences
Eissa Faqeih - King Fahd Medical City
Majed Aljeraisy - Riyadh, Saudi Arabia
Mohamed A. Hussein - King Saud bin Abdulaziz University for Health Sciences
Ali Alasmari - King Fahd Medical City
Majid Alfadhel - King Saud bin Abdulaziz University for Health Sciences
Publication Details: BMC pediatrics, Vol.19(1), pp.195-195
Publisher: BioMed Central
Grant note: ;
Identifiers: 9920675108331
Academic Unit: King Abdulaziz University; King Saud University; King Saud Bin Abdulaziz University for Health Sciences
Language: English
Resource Type: Journal article