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Ornithine transcarbamylase deficiency: a model for gene therapy
Journal article   Peer reviewed

Ornithine transcarbamylase deficiency: a model for gene therapy

M A Morsy and C T Caskey
Advances in experimental medicine and biology, Vol.368, pp.145-154
1994
PMID: 7741006

Abstract

Animals Genetic Therapy Humans Metabolism, Inborn Errors - enzymology Metabolism, Inborn Errors - genetics Metabolism, Inborn Errors - therapy Ornithine Carbamoyltransferase - genetics Ornithine Carbamoyltransferase Deficiency Disease Urea - metabolism

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